Blog

Bluebird Bio's sickle cell gene therapy working for French boy

By Ben Hirschler LONDON (Reuters) – A pioneering gene therapy for sickle cell disease is working well so far for a 13-year-old French boy with the hereditary blood disorder, researchers said on Saturday, in a boost for the technology to fix faulty genes. SCD is caused by a mutated gene, resulting in abnormal red blood cell function. Patients suffer anemia, painful obstruction of blood vessels and, in some cases, early